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2020

  • Miwa S, Watabe A, Shimada Y, Higuchi T,  Kobayashi H, Fukuda T, Kato F, Ida H, Ohashi T. Efficient engraftment of genetically modified cells is necessary to ameliorate central nervous system involvement of murine model of mucopolysaccharidosis type II by hematopoietic stem cell targeted gene therapy. Mol Genet Metab. 2020; 130(4):262-273. https://pubmed.ncbi.nlm.nih.gov/32631737/
  • Nojiri A, Anan I, Morimoto S, Kawai M, Sakuma T, Kobayashi M, Kobayashi H, Ida H, Ohashi T, Eto Y, Shibata T, Yoshimura M, Hongo K. Clinical findings of gadolinium-enhanced cardiac magnetic resonance in Fabry patients. J Cardiol. 2020; 75(1): 27-33. https://pubmed.ncbi.nlm.nih.gov/31623930/
  • Narita I, Ohashi T, Sakai N, Hamazaki T, Skuban N, Castelli JP, Lagast H, Barth JA. Efficacy and safety of migalastat in a Japanese population: a subgroup analysis of the ATTRACT study. Clin Exp Nephrol. 2020; 24(2): 157-66. https://pubmed.ncbi.nlm.nih.gov/31889231/
  • Wada M, Shimada Y, Izuka S, IshiiN, Hiraki H, Tachibana T, Maeda K, Saito M, Arakawa S, Ishimoto T, Ida H, Ohashi T, Kobayashi H.  Ex vivo gene therapy treats bone complications of mucopolysaccharidosis typeII mouse models through bone remodeling reactivation. Mol Ther Methods Clin Dev. 2020; 19: 261-274. https://pubmed.ncbi.nlm.nih.gov/33102618/
  • Tsunogai T, Yamaoka M, Ohyama W,Honda T, Kusuhara A, Akiyama M. Aggressive B-Cell lymphoma involving the appendix and bilateral ovaries in an 11-Year-Old Girl. J Pediatr Adolesc Gynecol.2020; 33(4):421-424. https://pubmed.ncbi.nlm.nih.gov/32304857/
  • Feldt-Rasmussen U, Hughes D, Sunder-Plassmann G, Shankar S, Nedd K, Olivotto I, Ortiz D, Ohashi T, Hamazaki T, Skuban N, Yu J, Barth JA, Nicholls K. Long-term efficacy and safety of migalastat treatment in Fabry disease: 30-month results from the open-label extension of the randomized, phase 3 ATTRACT study. Mol Genet Metab. 2020;131(1-2):219-228. https://pubmed.ncbi.nlm.nih.gov/33012654/